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Results 2025 iGEM · SYPHU-CHINA

Complete ATRA biosynthetic pathway in E. coli: from gene cloning to functional validation.


Executive Summary

Summary. We established a complete biosynthetic route for all-trans retinoic acid (ATRA) in E. coli, covering PCR amplification, plasmid assembly, protein expression, pathway integration, lactate-responsive regulation, and stability evaluation.
  • Full genetic stack: all key genes amplified and verified; upstream β-carotene and downstream retinal→ATRA modules constructed and co-expressed.
  • Strong chassis performance: high transformation efficiency; robust enzyme expression.
  • Functional outputs: β-carotene (upstream) and ATRA (combined strain) detectable.
  • Smart control: lactate-responsive induction with wide dynamic range in a physiologically relevant window.
  • Operability: plasmid retention >90% over 20 generations under our conditions.

Gene Amplification and Verification

Goal. Obtain clean, size-correct PCR products to maximize downstream assembly efficiency.

Gene Amplification Analysis

Figure A. Gene amplification analysis (gene-amplification-analysis). Representative gels and QC summaries for the four pathway genes.

Interpretation: Band sizes match theoretical lengths within tolerance; A260/A280 indicates high nucleic-acid purity suitable for cloning.

Analytical summary of PCR products
Gene Theoretical size Experimental size Concentration (ng/μL) Purity (A260/A280) Amplification efficiency (%)
blhSR1,812 bp1,809 ± 745.2 ± 3.11.87 ± 0.0394.3 ± 2.1
raldhHS1,521 bp1,518 ± 538.7 ± 2.81.85 ± 0.0296.1 ± 1.8
IIdR897 bp894 ± 452.1 ± 4.21.89 ± 0.0497.8 ± 1.2
crtEBIY5,214 bp5,198 ± 1228.3 ± 2.51.83 ± 0.0585.4 ± 3.5

Plasmid Construction and Verification

Strategy. Homologous recombination for upstream (crtEBIY) and downstream (blhSR–raldhHS) modules; validated by colony PCR and sequencing.

Plasmid Quality Analysis

Figure B. Plasmid quality analysis (plasmid-quality-analysis). Concentration, purity indices and functional colony screens.

Interpretation: High A260/A230 & A260/A280 and >108 CFU/μg transformation support plasmid integrity; positive-clone rate >88% confirms efficient assembly.

Plasmid construct Conc. (ng/μL) A260/A280 A260/A230 Transform. efficiency (CFU/μg) Positive clones (%)
Downstream pathway68.5 ± 5.21.86 ± 0.022.15 ± 0.05(2.8 ± 0.3)×10⁸92 ± 3
Upstream pathway72.3 ± 4.81.84 ± 0.032.12 ± 0.07(2.5 ± 0.2)×10⁸88 ± 4
Acceptance criteria>501.8–2.0>2.0>1×10⁸>80

Protein Expression and Functional Characterization

Result. SDS-PAGE confirmed robust expression at expected MW. Induction at 25–30 °C balanced total expression and solubility.

Temperature Optimization Analysis

Figure C. Temperature optimization (temperature-optimization-analysis). Solubility vs. total expression across induction temperatures.

Interpretation: 25–30 °C yields the best compromise for active enzymes supporting downstream flux.

Expression & activity metrics
EnzymeTheor. MW (kDa)ExpressionSolubilitySpecific activity (U/mg)Note
BlhSR67.8Strong68 ± 5% soluble12.3 ± 1.2Drives retinal formation
RALDH55.1Strong75 ± 4% soluble8.7 ± 0.9Terminal oxidation to ATRA
CrtE/B/I/Y20–44ModerateMembrane-associatedN/Aβ-carotene confirmed

Metabolic Pathway Functionality

Outcome. Flux from β-carotene to retinal and ATRA was confirmed using phenotype and LC–MS quantification.

Static Metabolic Pathway

Figure D. Static metabolic pathway (static-metabolic-pathway). Upstream carotenoid & downstream retinoid modules overview.

Context: The schematic maps measured intermediates to specific enzymatic steps.

Metabolite Production Analysis

Figure E. Metabolite production (metabolite-production-analysis). Module-wise outputs vs full pathway.

Interpretation: Retinal >> ATRA implies RALDH oxidation is rate-limiting → priority for enzyme/cofactor engineering.

Production Kinetics Analysis

Figure F. Production kinetics (production-kinetics-analysis). Growth-associated β-carotene formation across 24 h.

Interpretation: Peak volumetric productivity near transition to stationary phase → informs induction timing for fed-batch.

Time-course (24 h) table
Time (h)OD600β-Carotene (mg/L)Vol. productivity (mg·L⁻¹·h⁻¹)Specific yield (mg/OD)
00.65 ± 0.050.05 ± 0.010.08
61.82 ± 0.080.38 ± 0.060.0550.21
122.95 ± 0.121.12 ± 0.150.1230.38
183.42 ± 0.151.89 ± 0.220.1280.55
243.68 ± 0.182.35 ± 0.320.0770.64

Lactate-Responsive Regulation

Relevance. Tumor-like lactate levels (1–10 mM) trigger a strong, selective induction with acceptable viability.

Lactate Induction Analysis

Figure G. Lactate induction (lactate-induction-analysis). Dose–response across a physiological window.

Interpretation: Response window overlaps tumor microenvironment; supports in situ activation concepts.

Temporal activation after induction
Time (min)Protein (%)mRNA (rel.)Apparent translationState
01001001.00Baseline
15185 ± 12220 ± 150.84Initial
30420 ± 25580 ± 320.72Accumulation
60720 ± 35850 ± 420.85Near-max
120870 ± 28920 ± 380.95Steady

Genetic Stability

Finding. High plasmid retention and functionality across serial passages; suitable for batch and short continuous runs.

GenerationPlasmid retention (%)Functional expression (%)Segregational loss (%/gen)Specific productivity (rel.)
0100100100
598 ± 197 ± 20.4097
1096 ± 294 ± 30.4194
1594 ± 291 ± 30.4391
2092 ± 388 ± 40.4588

Interpretation: For very long continuous processes, consider genomic integration or addiction systems to further reduce segregational loss.


Key Performance Indicators

Visualization set. Bubble chart for milestone impact, 3D response surface for interaction effects, parallel coordinates for multi-objective trade-offs.

Performance Metrics Bubble Chart

Figure H. Performance metrics bubble chart (static-bubble-chart). Compact view of milestones vs relative impact.

Interpretation: Bubble size/position highlight key contributors (e.g., cloning efficiency, inducible control range).

3D Response Surface

Figure I. 3D response surface (3d-response-surface). Output predicted across two interacting factors under fixed constraints.

Interpretation: A ridge emerges at moderate induction and mid-temperature, consistent with wet-lab screens.

Parallel Coordinates Optimization

Figure J. Parallel-coordinates optimization (parallel-coordinates-optimization). Feasible regions satisfying yield, stability and viability constraints.

Interpretation: Guides DBTL cycles by exposing trade-offs and Pareto-like fronts.

KPI summary table
MetricTargetAchievedRatingSignificance
Gene cloning100%100%ExcellentFoundation for DBTL cycles
Plasmid construction>80%90%ExcellentFaster iteration
Transformation>10⁸ CFU/μg2.8×10⁸ExceededLibrary readiness
Protein expressionDetectableStrongExcellentFunctional capacity
β-CaroteneDetectable2.35 mg/LAchievedUpstream validated
ATRADetectable28.4 nMAchievedFull pathway confirmed
Induction range>5-fold8.7-foldExcellentPrecise control
Stability (20 gen)>80%92%ExceededScale-up feasibility

Analysis and Discussion

Technical achievements
  • Complete pathway integration with detectable ATRA output.
  • High-efficiency cloning & recombination framework (>90% positive clones).
  • Lactate-responsive circuit with large dynamic range.
  • Kinetic profiling informs temperature and induction set-points.
System insights
  • 25–30 °C balances solubility and expression for active yield.
  • RALDH oxidation appears rate-limiting (retinal accumulation).
  • Low segregational loss suggests manageable burden across passages.
Translational potential
  • Sustainable ATRA bioproduction complementing chemical synthesis.
  • Environment-responsive control for tumor-localized activation concepts.
  • Platform extensibility to other retinoids.

Conclusion

We reconstructed an end-to-end ATRA pathway in E. coli and validated each layer—genetics, expression, metabolism, regulation, and stability. While yield optimization remains, these results establish a robust framework for further engineering and application.
All experiments followed iGEM safety guidelines and institutional biosafety protocols. Complete procedures and raw data are available upon request.
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